Autism Spectrum Disorder

Autism affects millions, yet families face few treatment options—often navigating trial-and-error care without FDA-approved therapies or accessible support.

Precision therapy for Autism


Piton is developing pharmacologic therapies to restore a common metabolic deficiency in autistic individuals - to improve quality of life.

The science behind our Autism Spectrum Disorder program


At Piton Therapeutics, we leverage large, multi-modal patient cohorts to discover efficacious treatments for broad patient populations.

Our solution


PTX-2009 is a small molecule that works through the gut microbiota to provide molecules critical for neurodevelopment.

Find out more about our Autism program


At Piton Therapeutics, we are revolutionizing precision medicine through our state-of-the-art AI-powered platform, unlocking novel small-molecule therapeutics with unparalleled specificity.